Dyne Therapeutics’ DYNE-251 Gains Orphan Drug Status in Japan for Duchenne Muscular Dystrophy Read more
Er-Kim and Sentynl Therapeutics Partner to Expand Access to Rare Disease Treatments in EMEA and Eurasian Markets Read more
Biostar Pharma’s Utidelone Receives Third Orphan Drug Designation from FDA for Pancreatic Cancer Read more