Andelyn Biosciences and Amplo Biotech Partner to Advance Gene Therapies for Neuromuscular Junction Disorders Read more
DAWNZERA (donidalorsen) Becomes First FDA-Approved RNA-Targeted Prophylactic for Hereditary Angioedema Read more
FDA Grants Orphan Drug Designation to Crinetics’ Atumelnant for Congenital Adrenal Hyperplasia Read more